New insights into the evaluation of randomized controlled trials for rare diseases over a long-term research horizon: a simulation study

New insights into the evaluation of randomized controlled trials for rare diseases over a long-term research horizon: a simulation study. Bayar, M. A.; Le Teuff, G.; Michiels, S.; Sargent, D. J.; Le Deley, M. C.. Stat Med. 2016; 3245-58: p.3245-58. doi:10.1002/sim.6942 10.1002/sim.6942. Epub 2016 Mar 30.

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